29th European Hematology Association Congress

• EHA •
• 14 June, 2024 •
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A Phase 3, Randomised, Double-Blind, Placebo-controlled Trial to Evaluate the Efficacy and Safety of Avatrombopag for the Treatment of Thrombocytopenia in Paediatric Subjects with Immune Thrombocytopenia (AVA-PED-301)

Rachael F. Grace, Göksel Leblebisatan, Yesim Aydinok, Şule Ünal, John Grainger, Jessica Zhang, Linda Smallwood, Emily de León, Brian D. Jamieson

Available materials

• EHA •
• 14 June, 2024 •
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A European retrospective study to describe real-world outcomes, treatment patterns and resource use in primary idiopathic thrombocytopenic purpura patients treated with avatrombopag: Interim results

Francesco Zaja, Quentin Hill, Fiona Glen, Fatemeh Saberi Hosnijeh, Luca Le Treust, Lara Groves, Milica Putnik, Carly Rich

• EHA •
• 14 June, 2024 •
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Impact of thrombopoietin receptor agonists and adherence to instructions for treatment of chronic primary immune thrombocytopenia: interim results of a real-world cross-sectional international survey

Srikanth Nagalla, Cecilie Yssing, Donatella Decise, Milica Putnik, Carly Rich

• EHA •
• 14 June, 2024 •
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Real-World Treatment Patterns and Outcomes in Patients with Immune Thrombocytopenia Treated with Avatrombopag in the United States: REAL-AVA 2.0 Interim Analysis Results

Srikanth Nagalla, My Levy, Shruti Chaturvedi, Abiola Oladapo, Chelsea Bernheisel, Elyse Swallow, Debbie Goldschmidt, Alexandra Greatsinger, Kirthana Sarathy, Loren Ormenaj, Michael Vredenburg , Scott Kolodny

• EHA •
• 14 June, 2024 •
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Results of a Phase 4, Prospective, Open-label, Study Evaluating the Safety, Efficacy, and Treatment Satisfaction in Adult Chronic Immune Thrombocytopenia (ITP) Subjects after Switching to Avatrombopag (AVA) from Eltrombopag (ELT) or Romiplostim (ROMI)

Michael Tarantino, Scott Kolodny, Jessica Zhang, Brian Jamieson, Michael Vredenburg

• EHA •
• 13 June, 2024 •
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A retrospective analysis of pacritinib treatment outcomes in myelofibrosis patients with and without monocytosis

Eric Padron, Mrinal Patnaik, Daniel Wiseman, Raphael Itzykson, Douglas Tremblay, John Mascarenhas, Sarah Buckley, Karisse Roman-Torres, Michael R. Savona

Available materials

• EHA •
• 13 June, 2024 •
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Phase 4 ADOPT study: interim analysis of efficacy and safety results of avatrombopag treatment in adult patients with immune thrombocytopenia

María Teresa Álvarez Román, María Luisa Lozano, Wolfgang Miesbach, Hafiz Qureshi, Vickie McDonald, Jessica Zhang, Milica Putnik, Viridiana Cano Garcia, Brian Jamieson, Stefan Lethagen, María Eva Mingot Castellano

Available materials

• EHA •
• 13 June, 2024 •
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Injection Site Reactions in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria Who Received Subcutaneous Pegcetacoplan Monotherapy for Up to 3 Years

Louise M Arnold, Barbara Czech, Peter Hillmen, Richard J. Kelly

• EHA •
• 13 June, 2024 •
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Long-term outcomes of pegcetacoplan treatment in patients with paroxysmal nocturnal hemoglobinuria and baseline hemoglobin levels greater than 10 grams per deciliter

Jens Panse , Régis Peffault de Latour, Johan Szamosi, Regina Horneff, Peter Hillmen, Raymond Siu Ming Wong

Available materials

• EHA •
• 13 June, 2024 •
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Thrombosis and Meningococcal Infection Rates in Pegcetacoplan Patients With Paroxysmal Nocturnal Hemoglobinuria in the Post-marketing Setting

Jens Panse , Richard J. Kelly, Hisakazu Nishimori, Regina Horneff, Peter Hillmen, Uchendu O. Uchendu, Stacie Lallier, Gloria F Gerber

Available materials

• EHA •
• 13 June, 2024 •
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Efficacy and safety of intensive pegcetacoplan dosing for the treatment of acute hemolysis in patients with paroxysmal nocturnal hemoglobinuria

Morag Griffin, Christopher Patriquin, Kensuke Usuki, Elena Surova, Johan Szamosi, Uchendu O. Uchendu, Jeff Szer

Available materials

• EHA •
• 13 June, 2024 •
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Characterization of clinically significant breakthrough hemolysis in patients with paroxysmal nocturnal hemoglobinuria treated with pegcetacoplan

Régis Peffault de Latour, Carlos de Castro, Brian Mulherin, Christopher Patriquin, Veena Selvaratnam, Richard J. Kelly, Morag Griffin, Elena Surova, Johan Szamosi, Uchendu O. Uchendu, Raymond Siu Ming Wong

Available materials

• EHA •
• 13 June, 2024 •
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Improvement in Iron Overload With Pegcetacoplan Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria Previously Treated With Eculizumab

Jamille Shammo, Michael Yeh, Peter Hillmen, David J Kuter

Available materials