Study funded by Sobi and Sanofi.

Link to Online-Publication-Only Abstract

Publication
  • ASH •
  • 9 December, 2024 •
  • •

Association Between Hemophilia Joint Health Score and Quality of Life Using Results from the XTEND-1 Efanesoctocog Alfa Phase 3 Trial

Christoph Königs, Doris V. Quon, Cedric Hermans, Nana Kragh, Jérôme Msihid, Emilie Gerard, Duygu Bozkaya, Linda Bystrická, Cecile LeCamus, Elena Santagostino, Annemieke Willemze, Annette von Drygalski

Publication
  • ASH •
  • 9 December, 2024 •
  • •

Real-World Paterns of Additional Factor Treatment Use Among Hemophilia A Patients on Regular Prophylaxis in the United States: Results from the PicnicHealth database

Jonathan C. Roberts, Angela Weyand, Mark Reding, Nana Kragh, Nicole Tsao, Emily Cibelli, Gillian Hanson, Duygu Bozkaya, Anne-Laure Tardy

Publication
  • ASH •
  • 9 December, 2024 •
  • •

Unmet Needs, Factor Consumption, and Healthcare Resource Use among People with Hemophilia A: Real-World Analysis of the Adelphi Hemophilia Disease Specific Programme™

Lynn Malec, Davide Matino, Kieran Wynne-Cattanach, Chris Blazos, Duygu Bozkaya, Anne-Laure Tardy, Jennifer Dumont , Sylvie Bozzi

Publication
  • ASH •
  • 9 December, 2024 •
  • •

Use of Avatrombopag in Patients with Immune Thrombocytopenia: Interim Analysis of the Phase 4 ADOPT Study

María Eva Mingot Castellano, María Teresa Álvarez Román, María Luisa Lozano, Wolfgang Miesbach, Hafiz Qureshi, Vickie McDonald, Milica Putnik, Jessica Zhang, Viridiana Cano Garcia, Nina Skuban, Stefan Lethagen

Publication
  • ISTH •
  • 24 June, 2025 •
  • •

Major Surgical Outcomes with Efanesoctocog Alfa: 4 Years’ Experience in the XTEND Clinical Program

Liane Khoo, Robert Klamroth, Annette von Drygalski, Sandrine Meunier, Davide Matino, Umer Khan, Elena Santagostino, Lara Mamikonian, Linda Bystrická, Graham Neill, Flora Peyvandi

Available materials

Oral Presentation
Publication
  • ISTH •
  • 24 June, 2025 •
  • •

Long-term observational joint health study in patients initiating efanesoctocog alfa: baseline data

Jonathan C. Roberts, Larissa Bornikova, Eric Grabowski, Amit Soni, Jennifer Dumont, Charlotte Sensinger, Nicole Tsao

Available materials

Poster
Publication
  • ISTH •
  • 24 June, 2025 •
  • •

Observational Study of Prophylactic Efanesoctocog Alfa for Joint Health in Hemophilia A: PROTECT-ALT

Te-Fu Weng, Yi-Chih Hsu, Chih-Wei Lee, Da-Ming Yeh, Tong-Ling Chien, Nicole Tsao, Ching-Min Chang

Available materials

Poster
Publication
  • ISTH •
  • 24 June, 2025 •
  • •

Joint health outcomes with efanesoctocog alfa in adults/adolescents from XTEND-1 continuing XTEND-ed

Christoph Königs, Annette von Drygalski, Cedric Hermans, Barbara A. Konkle, Paul Van der Valk, Liane Khoo, Nobuaki Suzuki, Erin Feng, Umer Khan, Linda Bystrická, Jennifer Dumont, Elena Santagostino, Lara Mamikonian, Robert Klamroth

Available materials

Poster
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