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Medical materials

Publication
  • ISTH
  • 25 June, 2024

First Interim Analysis of Clinical Outcomes in Adults and Adolescents With Severe Hemophilia A Receiving Efanesoctocog Alfa Prophylaxis in XTEND-ed, a Phase 3 Long-term Extension Study

Sophie Susen, Stephanie P’ng, Toshko Lissitchkov, Davide Matino, Pratima Chowdary, Angela Weyand, Robert Klamroth, Young-Shil Park, María Teresa Álvarez Román, Liqi Feng, Helena Palmborg, Jennifer Dumont , Elena Santagostino, Lila-Sabrina Fetita, Keiji Nogami

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Publication
  • ISTH
  • 25 June, 2024

Long-term Outcomes With Efanesoctocog Alfa Prophylaxis for Previously Treated Children With Severe Hemophilia A, an Interim Analysis of the Phase 3 XTEND-ed Study

Lynn Malec, Beatrice Nolan, Anthony KC Chan, Manuela Albisetti, Sheng-Chieh Chou, Bulent Zulfikar, Mindy Simpson, Liqi Feng, Helena Palmborg, Graham Neill, Lydia Abad-Franch, Sriya Gunawardena, Karin Fijnvandraat

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Publication
  • ISTH
  • 23 June, 2024

Perioperative Management with Efanesoctocog Alfa in Adults, Adolescents, and Children with Severe Hemophilia A in the Phase 3 XTEND Clinical Program

Anthony KC Chan, Sophie Susen, Liane Khoo, Annette von Drygalski, Johannes Oldenburg, Ming-Ching Shen, Flora Peyvandi, Cristina Tarango, Pratima Chowdary, Lara Mamikonian, Helena Palmborg, Jennifer Dumont , Elena Santagostino, Cedric Hermans

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Publication
  • ISTH
  • 22 June, 2024

Long-Term Joint Health Outcomes With a Recombinant Factor VIII Fc From the 48-Month Prospective, Observational A-MORE Study: Third Interim Analysis of Up to 24 Months

Jan Astermark, Johannes Oldenburg, Ruben Berrueco, Annarita Tagliaferri, Mikaela Alenäs, Markus Fusser, Stefan Lethagen

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Publication
  • ISTH
  • 22 June, 2024

Effectiveness and safety of efmoroctocog alfa (a recombinant factor VIII Fc) across body mass index (BMI) categories: Pooled data from two non-interventional phase 4 studies (A-SURE/PREVENT)

Johannes Oldenburg, María Teresa Álvarez Román, Anna-Elina Lehtinen, Markus Fusser, Sabine Lauer, Stefan Lethagen

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Publication
  • ISTH
  • 22 June, 2024

Using the Hemophilia Functional Ability Scoring Tool (Hemo-FAST) to describe the joint health status in adults with hemophilia

Virginie Barbay, Claude Négrier, Eva Bednar, Nana Kragh, Corinne Gandossi, Meriem Zidi, Aurelien Lebreton

Available materials

Publication
  • ISTH
  • 22 June, 2024

Interim Analysis of Joint Outcomes in Adult and Adolescent Patients With Severe Hemophilia A Receiving Efanesoctocog Alfa During the Phase 3 XTEND-ed Long-Term Extension Study

Annette von Drygalski, Christoph Königs, Barbara A. Konkle, Cedric Hermans, Liane Khoo, Kathelijn Fischer, Nobuaki Suzuki, Hailing Guo, Umer Khan, Linda Bystrická, Alejandro Fernandez, Elena Santagostino, Lara Mamikonian, Robert Klamroth

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