Sobi™ Satellite Symposium

Agenda

The importance of real-world experience and patient perspective in rare diseases - Danny Hsu, Australia (Chair)
PNH: Lifting the fog of fatigue - Ana Boban, Croatia
Common themes across rare haematological diseases: My observations from treating patients with PNH & ITP- Danny Hsu, Australia
ITP: Beyond the count, transforming patient care - María L Lozano, Spain
Panel discussion and conclusion - All Faculty

Publication
  • EHA •
  • 13 June, 2026 •
  • •

Consistency of Response by Baseline Platelet Count in Pacritinib-treated patients in the Real World: MY-PAC Analysis

James Rossetti, Douglas Tremblay, Abiola Oladapo, Michael Marrone, Caleb Paydar, Djibril Liassou, Sarah A. Buckley, Purvi Suthar, Adina Geprifti, Michael Vredenburg , Bruce Feinberg, Naveen Pemmaraju

Available materials

Poster
Publication
  • EHA •
  • 13 June, 2026 •
  • •

Avatrombopag in TPO RA–naive adults in acute, persistent, and chronic phases of ITP: results from the REAL AVA 3.0 retrospective study

Sandhya Panch, Abiola Oladapo, Faizan Sattar, Michael Vredenburg , Sarah Lucht, Emily Bland, Prathamesh Pathak, Bruce Feinberg, Debbie Jiang

Available materials

Poster
Publication
  • EHA •
  • 13 June, 2026 •
  • •

Real-world hemoglobin profiles and transfusion burden in patients with paroxysmal nocturnal hemoglobinuria receiving complement inhibitors: A US claims analysis

Carlos de Castro, Peter Blandino, Fiston Vuvu, Enrico Zanardo, Lynn Huynh, Robert Schell, Nathaniel Downes, Yixin Yang, Mei Sheng Duh, Peter Hillmen

Available materials

Poster
Publication
  • ERA •
  • 4 June, 2026 •
  • •

Decreasing rates of injection site reactions over time: Long-term outcomes across multiple indications support pegcetacoplan for C3G/primary IC-MPGN

Nabil Melhem, Antonio Mastrangelo, Daniel Zecher, Abdallah S Geara, Carla M Nester, Sheena Patel, Liza Alkhori Franzén, Andrew Carrel, Carlos de Castro, Daniel P Gale, Richard J. Kelly

Available materials

Oral Presentation
Publication
  • ASH •
  • 8 December, 2025 •
  • •

Real-World Clinical Characteristics and Treatment Outcomes in PNH Patients Prescribed Pegcetacoplan: Insights of Complement Inhibitor-Experienced and -Naïve Patients Across Europe, the United States and Canada  

Jens Panse , Koo Wilson, Brianne Kerr, Sam Williamson, Susanna Libby, Yasmin Taylor, Peter Hillmen, David Dingli

Publication
  • ASH •
  • 8 December, 2025 •
  • •

Patient-reported outcomes of avatrombopag for chronic immune thrombocytopenia: Interim analysis of the Phase 4 adopt study

María Eva Mingot Castellano, María Teresa Álvarez Román, María Luisa Lozano, Wolfgang Miesbach, Hafiz Qureshi, Vickie McDonald, Jessica Zhang, Viridiana Cano Garcia, Nina Skuban

Publication
  • ASH •
  • 7 December, 2025 •
  • •

Early Results From the Ongoing Pegcetacoplan Silo of the International Paroxysmal Nocturnal Hemoglobinuria Interest Group Registry 

Carlos de Castro, Peter Hillmen, Peter Blandino, David Araten

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